Design and analysis of clinical trials for small rare disease populations
نویسندگان
چکیده
Design and analysis of clinical trials for small rare disease populations Ralf‐Dieter Hilgers1*, Franz König2, Geert Molenberghs3 and Stephen Senn4 1Department of Medical Statistics, RWTH Universit Aachen, Pauwelstr 30, D‐ 52074 Aachen, Germany 2Center for Medical Statistics, Informatics and Intelligent Systems, Medical University of Vienna, Vienna, Austria 3I‐BioStat, Universiteit Hasselt, B‐3590 Diepenbeek, Belgium 4Competence Centre for Methodology and Statistics, Luxembourg Institute of Health, L‐1445 Strassen, Luxembourg
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